- Investigator
- Carmen Leon Astudillo
- Status
- Accepting Candidates
Friedreich ataxia
Our locations
Our Experts
Clinical Trials: Friedreich ataxia
BOB体育 research scientists make medicine better every day. They discover new ways to help people by running clinical trials. When you join a clinical trial, you can get advanced medical care. Sometimes years before it's available everywhere. You can also help make medicine better for everyone else. If you'd like to learn more about clinical trials, visit our clinical trials page. Or click one of the links below:
- Status
- Accepting Candidates
To evaluate the safety and tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of subcutaneous (SC) administration of CTI-1601 over 28 days in subjects with Friedreich's ataxia (FRDA).
- Investigator
- Sub Subramony
- Status
- Accepting Candidates
- Ages
- 18 Years - N/A
- Sexes
- All
News and Patient Stories: Friedreich ataxia
International advocacy group GoFAR funds BOB体育 research for Friedreich鈥檚 ataxia gene therapy program
April 19, 2018
University of Florida Health pediatrics researchers have received a $450,000 grant from the Italian patient advocacy group GoFAR to continue developing a gene鈥�
Department of Pediatrics, +4 more
UF and GoFAR announce gene therapy program for Friedreich鈥檚 ataxia
September 13, 2016
For media inquiries in the U.S., please call Mindy Cameron at 317-853-6294 or email: [email protected] . For media inquiries in EU, please contact Annaluisa鈥�
Clinical and Translational Science Institute, +2 more